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Tackling the challenges of lysosomal storage diseases diagnosis and treatment

by Chandré Blignaut | Feb 28, 2023 | Featured, News

Tackling the challenges of lysosomal storage diseases diagnosis and treatment A disease is defined as ’rare’ when it affects fewer than 1 in 2 000 people,1 and there are currently more than 7 000 known rare diseases (lysosomal storage diseases), affecting more than...
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